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$15.03
-3.22%
2026-09-03 16:00:01 EDT-$0.50
Healthcare
Biotechnology
NASDAQ
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Design Therapeutics, Inc. is a biopharmaceutical company in the preclinical phase that focuses on creating treatments for genetic conditions stemming from nucleotide ...

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$15.03
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Design Therapeutics, Inc. is a clinical-stage biopharmaceutical company headquartered in Carlsbad, California, founded in 2017 by Pratik Shah and Aseem Ansari. The company focuses on developing a new class of small molecule therapies, known as GeneTAC (Gene Targeted Chimera) molecules, designed to address the root cause of serious genetic diseases ...Design Therapeutics, Inc. is a clinical-stage biopharmaceutical company headquartered in Carlsbad, California, founded in 2017 by Pratik Shah and Aseem Ansari. The company focuses on developing a new class of small molecule therapies, known as GeneTAC (Gene Targeted Chimera) molecules, designed to address the root cause of serious genetic diseases resulting from nucleotide repeat expansions. These expansions are responsible for over 50 monogenic disorders, including Friedreich's Ataxia (FA), Myotonic Dystrophy Type-1 (DM1), Fragile X syndrome, spinocerebellar ataxias, Huntington's disease, and others. By targeting the underlying genetic defect, Design aims to provide functional cures rather than symptomatic relief. The company's lead programs are in Friedreich's Ataxia and Myotonic Dystrophy Type-1, with ongoing IND-enabling studies and a robust preclinical pipeline. Design went public in March 2021, raising capital to advance its research. As of 2026, it employs 54 people and maintains a strong financial position with a market cap around $873 million, no debt, and significant cash reserves (cash per share $3.318). The company is led by CEO and co-founder Pratik Shah, Ph.D., and its scientific advisory board includes experts in genetics and drug development. Despite being in pre-revenue stage with negative operating margins, Design's strategic partnerships, such as with the Friedreich's Ataxia Research Alliance, and its innovative platform position it for potential breakthroughs. The company's commitment to patient access is demonstrated by its expanded access policy. With a pipeline targeting multiple serious genetic conditions and a focus on high unmet medical needs, Design Therapeutics aims to transform the treatment landscape for genetic disorders.
Founded
2017
Employees
55
CEO
Pratik Shah
Full Name
Design Therapeutics, Inc.
Sector
Healthcare
Industry
Biotechnology
ROE
-34.03%
Market Cap
$0.94B
Current Ratio
18.86
WACC
12.24%
ROIC
-35.71%

Contact Information

858 293 4900
6005 Hidden Valley Road, Carlsbad, CA 92011

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