Design Therapeutics, Inc. is a biopharmaceutical company in the preclinical phase that focuses on creating treatments for genetic conditions stemming from nucleotide ...
Design Therapeutics, Inc. is a clinical-stage biopharmaceutical company headquartered in Carlsbad, California, founded in 2017 by Pratik Shah and Aseem Ansari. The company focuses on developing a new class of small molecule therapies, known as GeneTAC (Gene Targeted Chimera) molecules, designed to address the root cause of serious genetic diseases ...Design Therapeutics, Inc. is a clinical-stage biopharmaceutical company headquartered in Carlsbad, California, founded in 2017 by Pratik Shah and Aseem Ansari. The company focuses on developing a new class of small molecule therapies, known as GeneTAC (Gene Targeted Chimera) molecules, designed to address the root cause of serious genetic diseases resulting from nucleotide repeat expansions. These expansions are responsible for over 50 monogenic disorders, including Friedreich's Ataxia (FA), Myotonic Dystrophy Type-1 (DM1), Fragile X syndrome, spinocerebellar ataxias, Huntington's disease, and others. By targeting the underlying genetic defect, Design aims to provide functional cures rather than symptomatic relief. The company's lead programs are in Friedreich's Ataxia and Myotonic Dystrophy Type-1, with ongoing IND-enabling studies and a robust preclinical pipeline. Design went public in March 2021, raising capital to advance its research. As of 2026, it employs 54 people and maintains a strong financial position with a market cap around $873 million, no debt, and significant cash reserves (cash per share $3.318). The company is led by CEO and co-founder Pratik Shah, Ph.D., and its scientific advisory board includes experts in genetics and drug development. Despite being in pre-revenue stage with negative operating margins, Design's strategic partnerships, such as with the Friedreich's Ataxia Research Alliance, and its innovative platform position it for potential breakthroughs. The company's commitment to patient access is demonstrated by its expanded access policy. With a pipeline targeting multiple serious genetic conditions and a focus on high unmet medical needs, Design Therapeutics aims to transform the treatment landscape for genetic disorders.
YoYYoY means Year-over-Year. It compares the latest annual value with the previous annual value to show long-term trend strength.
QoQQoQ means Quarter-over-Quarter. It compares the latest quarter with the immediately previous quarter to show short-term momentum changes.
RevenueThe total money that came through the front door from selling things, before paying a single bill. Think of it as the grand total of every credit card swipe from customers. (YoY compares this year to last year's performance, while QoQ compares the current three months to the previous three).
$0
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Net IncomeThe absolute bottom line. If the company paid every single supplier, employee, banker, and tax collector, this is the actual money left in their pocket at the end of the day.
$-69.8M
-40.7%
-14.3%
Gross MarginThe basic markup. If they sell a $100 pair of sneakers, this percentage tells you how much of that price tag is profit right after paying for the rubber and shoelaces, but before paying for things like store rent or TV commercials.
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Operating MarginThe 'day job' efficiency score. Out of every dollar a customer spends, this shows how many cents the company keeps after making the product AND paying for all the everyday corporate overhead (like salaries, marketing, and keeping the lights on).
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Net MarginThe final take-home percentage. When you strip away every conceivable cost, tax, and interest payment, this is the exact number of cents the company truly gets to keep from every dollar in sales.
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Free Cash FlowThe holy grail of corporate cash. It's the spendable, physical money left over after the business pays for its daily operations AND buys the big, expensive upgrades (like new factories or servers) it needs to survive. This is the 'free' money they can use to pay dividends or buy back stock.
$-54.6M
-25.6%
+5.4%
FCF MarginThe ultimate cash conversion rate. It shows how good the company is at turning regular sales directly into cold, hard, spendable cash. A high percentage means the business is an absolute cash-printing machine.
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Debt / EquityThe financial risk gauge. It compares how much of the company's empire was built using borrowed money (loans) versus the owners' own money (shareholders). A high number means they are heavily leveraged and playing a riskier game; a low number means they are playing it safe.
0.7%
-25.1%
-19.8%
Current RatioThe 12-month survival check. It simply compares the cash they have right now (plus things they can quickly turn into cash) against the immediate bills they absolutely must pay this year. A score above 1 means they have enough in the wallet to cover the upcoming bills without panicking.
17.14x
-41.5%
-15.3%
Total AssetsThe absolute size of the company's empire. It bundles together absolutely everything of value they own—from the cash in the register and the inventory in the warehouse, to the software patents in the vault and the factories on the ground.